Goal of this study

To treat Duchenne muscular dystrophy.



Duchenne muscular dystrophy (DMD) is a genetic disease due to the absence of a protein called dystrophin. DMD is characterized by progressive muscle degeneration and weakness, and is due to deterioration of muscle cells which are important for body movement. This study will investigate the efficacy and safety of a drug named Edasalonexent in patients with DMD. Edasalonexent will be given to the patient through the mouth three times daily every day for a period of 52 weeks.

Who can participate in this study?

Patients who have been diagnosed with Duchenne muscular dystrophy and who are between 4 and 7 years of age (up to the 8th birthday) may be eligible to participate in this study. This study accepts boys and does not accept healthy volunteers.

Important: Additional eligibility criteria apply and the patient’s record will be verified by the study doctor (with the patient’s approval) to confirm eligibility.


ClinicalTrials.gov Identifier: NCT03703882

Contact Information

To know if you're eligible to participate in this trial, please fill-up the form below and we will contact you shortly.